GENE THERAPY & RNAi-BASED THERAPY
Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. In practice, a non-functional/mutated gene is replaced with an engineered DNA molecule encoding a functional copy or a therapeutic protein. RNA interference (RNAi)-based therapy uses engineered RNA molecules to inhibit in vivo gene expression. In practice, the expression or injection of engineered RNA molecules work via mechanisms including transcript cleavage, sequestration, and inhibition of protein translation. Impactys provides a wide range of gene & RNAi-based therapeutic solutions, including: